Pressure for drug development in lysosomal storage disorders: a quantitative analysis thirty years beyond the US orphan drug act - Mechler, Konstantin; Hoffmann, Georg F.; Ries, Markus (BioMed Central, 2015)
Aus: Orphanet Journal of Rare Diseases, 10 (2015), Nr. 46. pp. 1-9. ISSN 1750-1172