Patisiran, an RNAi therapeutic, for hereditary transthyretin amyloidosis
Original Article from The New England Journal of Medicine - Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis
Guardado en:
| Autores principales: | , |
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| Formato: | Article (Journal) |
| Lenguaje: | inglés |
| Publicado: |
July 5, 2018
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| In: |
The New England journal of medicine
Year: 2018, Volumen: 379, Número: 1, Pages: 11-21 |
| ISSN: | 1533-4406 |
| DOI: | 10.1056/NEJMoa1716153 |
| Acceso en línea: | Verlag, Volltext: https://doi.org/10.1056/NEJMoa1716153 Verlag, Volltext: https://www.nejm.org/doi/10.1056/NEJMoa1716153 |
| Notas de Autor: | D. Adams, A. Gonzalez-Duarte, W.D. O’Riordan, C.-C. Yang, M. Ueda, A.V. Kristen, I. Tournev, H.H. Schmidt, T. Coelho, J.L. Berk, K.-P. Lin, G. Vita, S. Attarian, V. Planté-Bordeneuve, M.M. Mezei, J.M. Campistol, J. Buades, T.H. Brannagan III, B.J. Kim, J. Oh, Y. Parman, Y. Sekijima, P.N. Hawkins, S.D. Solomon, M. Polydefkis, P.J. Dyck, P.J. Gandhi, S. Goyal, J. Chen, A.L. Strahs, S.V. Nochur, M.T. Sweetser, P.P. Garg, A.K. Vaishnaw, J.A. Gollob, and O.B. Suhr |
| Sumario: | Original Article from The New England Journal of Medicine - Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis |
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| Notas: | Gesehen am 07.05.2019 |
| Descripción Física: | Online Resource |
| ISSN: | 1533-4406 |
| DOI: | 10.1056/NEJMoa1716153 |