Patisiran, an RNAi therapeutic, for hereditary transthyretin amyloidosis

Original Article from The New England Journal of Medicine - Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis

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Dettagli Bibliografici
Autori principali: Adams, David B. (Autore) , Kristen, Arnt (Autore)
Natura: Article (Journal)
Lingua:inglese
Pubblicazione: July 5, 2018
In: The New England journal of medicine
Year: 2018, Volume: 379, Fascicolo: 1, Pages: 11-21
ISSN:1533-4406
DOI:10.1056/NEJMoa1716153
Accesso online:Verlag, Volltext: https://doi.org/10.1056/NEJMoa1716153
Verlag, Volltext: https://www.nejm.org/doi/10.1056/NEJMoa1716153
Testo
Note sull'autore:D. Adams, A. Gonzalez-Duarte, W.D. O’Riordan, C.-C. Yang, M. Ueda, A.V. Kristen, I. Tournev, H.H. Schmidt, T. Coelho, J.L. Berk, K.-P. Lin, G. Vita, S. Attarian, V. Planté-Bordeneuve, M.M. Mezei, J.M. Campistol, J. Buades, T.H. Brannagan III, B.J. Kim, J. Oh, Y. Parman, Y. Sekijima, P.N. Hawkins, S.D. Solomon, M. Polydefkis, P.J. Dyck, P.J. Gandhi, S. Goyal, J. Chen, A.L. Strahs, S.V. Nochur, M.T. Sweetser, P.P. Garg, A.K. Vaishnaw, J.A. Gollob, and O.B. Suhr
Descrizione
Riassunto:Original Article from The New England Journal of Medicine - Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis
Descrizione del documento:Gesehen am 07.05.2019
Descrizione fisica:Online Resource
ISSN:1533-4406
DOI:10.1056/NEJMoa1716153