Patisiran, an RNAi therapeutic, for hereditary transthyretin amyloidosis
Original Article from The New England Journal of Medicine - Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis
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| Autori principali: | , |
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| Natura: | Article (Journal) |
| Lingua: | inglese |
| Pubblicazione: |
July 5, 2018
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| In: |
The New England journal of medicine
Year: 2018, Volume: 379, Fascicolo: 1, Pages: 11-21 |
| ISSN: | 1533-4406 |
| DOI: | 10.1056/NEJMoa1716153 |
| Accesso online: | Verlag, Volltext: https://doi.org/10.1056/NEJMoa1716153 Verlag, Volltext: https://www.nejm.org/doi/10.1056/NEJMoa1716153 |
| Note sull'autore: | D. Adams, A. Gonzalez-Duarte, W.D. O’Riordan, C.-C. Yang, M. Ueda, A.V. Kristen, I. Tournev, H.H. Schmidt, T. Coelho, J.L. Berk, K.-P. Lin, G. Vita, S. Attarian, V. Planté-Bordeneuve, M.M. Mezei, J.M. Campistol, J. Buades, T.H. Brannagan III, B.J. Kim, J. Oh, Y. Parman, Y. Sekijima, P.N. Hawkins, S.D. Solomon, M. Polydefkis, P.J. Dyck, P.J. Gandhi, S. Goyal, J. Chen, A.L. Strahs, S.V. Nochur, M.T. Sweetser, P.P. Garg, A.K. Vaishnaw, J.A. Gollob, and O.B. Suhr |
| Riassunto: | Original Article from The New England Journal of Medicine - Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis |
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| Descrizione del documento: | Gesehen am 07.05.2019 |
| Descrizione fisica: | Online Resource |
| ISSN: | 1533-4406 |
| DOI: | 10.1056/NEJMoa1716153 |