Enzyme replacement therapy with agalsidase alfa in patients with Fabry's disease: an analysis of registry data
Summary - Background - We analysed 5-year treatment with agalsidase alfa enzyme replacement therapy in patients with Fabry's disease who were enrolled in the Fabry Outcome Survey observational database (FOS). - Methods - Baseline and 5-year data were available for up to 181 adults (126 men) in...
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| Main Authors: | , |
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| Format: | Article (Journal) |
| Language: | English |
| Published: |
1 December 2009
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| In: |
The lancet
Year: 2009, Volume: 374, Issue: 9706, Pages: 1986-1996 |
| ISSN: | 1474-547X |
| DOI: | 10.1016/S0140-6736(09)61493-8 |
| Online Access: | Verlag, Volltext: https://doi.org/10.1016/S0140-6736(09)61493-8 Verlag, Volltext: http://www.sciencedirect.com/science/article/pii/S0140673609614938 
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| Author Notes: | A Mehta, M Beck, P Elliott, R Giugliani, A Linhart, G Sunder-Plassmann, R Schiffmann, F Barbey, M Ries, JTR Clarke, on behalf of the Fabry Outcome Survey investigators |