Enzyme replacement therapy with agalsidase alfa in patients with Fabry's disease: an analysis of registry data

Summary - Background - We analysed 5-year treatment with agalsidase alfa enzyme replacement therapy in patients with Fabry's disease who were enrolled in the Fabry Outcome Survey observational database (FOS). - Methods - Baseline and 5-year data were available for up to 181 adults (126 men) in...

Ausführliche Beschreibung

Gespeichert in:
Bibliographische Detailangaben
Hauptverfasser: Mehta, Atul B. (VerfasserIn) , Ries, Markus (VerfasserIn)
Dokumenttyp: Article (Journal)
Sprache:Englisch
Veröffentlicht: 1 December 2009
In: The lancet
Year: 2009, Jahrgang: 374, Heft: 9706, Pages: 1986-1996
ISSN:1474-547X
DOI:10.1016/S0140-6736(09)61493-8
Online-Zugang:Verlag, Volltext: https://doi.org/10.1016/S0140-6736(09)61493-8
Verlag, Volltext: http://www.sciencedirect.com/science/article/pii/S0140673609614938
Volltext
Verfasserangaben:A Mehta, M Beck, P Elliott, R Giugliani, A Linhart, G Sunder-Plassmann, R Schiffmann, F Barbey, M Ries, JTR Clarke, on behalf of the Fabry Outcome Survey investigators
Search Result 1

Enzyme replacement therapy with agalsidase alfa in patients with Fabry's disease: an analysis of registry data von Mehta, Atul B. (VerfasserIn) , Beck, Michael (VerfasserIn) , Elliott, P. (VerfasserIn) , Giugliani, R. (VerfasserIn) , Linhart, A. (VerfasserIn) , Sunder-Plassmann, Gere (VerfasserIn) , Schiffmann, Raphael (VerfasserIn) , Barbey, F. (VerfasserIn) ,


Volltext
Article (Journal)