Safety and efficacy of mTOR inhibitor treatment in patients with tuberous sclerosis complex under 2 years of age: a multicenter retrospective study

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Bibliographic Details
Main Authors: Saffari, Afshin (Author) , Brösse, Ines (Author) , Tilburg, Cornelis M. van (Author) , Hoffmann, Georg F. (Author) , Kölker, Stefan (Author) , Witt, Olaf (Author) , Milde, Till (Author) , Ziegler, Andreas (Author) , Syrbe, Steffen (Author)
Format: Article (Journal) Book/Monograph
Language:English
Published: London BioMed Central 2019
Heidelberg Universitätsbibliothek Heidelberg 2019
Online Access:Resolving-System, kostenfrei, Volltext: https://nbn-resolving.de/urn:nbn:de:bsz:16-heidok-264004
Verlag, kostenfrei, Volltext: http://www.ub.uni-heidelberg.de/archiv/26400
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Author Notes:Afshin Saffari, Ines Brösse, Adelheid Wiemer-Kruel, Bernd Wilken, Paula Kreuzaler, Andreas Hahn, Matthias K. Bernhard, Cornelis M. van Tilburg, Georg F. Hoffmann, Matthias Gorenflo, Sven Hethey, Olaf Kaiser, Stefan Kölker, Robert Wagner, Olaf Witt, Andreas Merkenschlager, Andreas Möckel, Timo Roser, Jan-Ulrich Schlump, Antje Serfling, Juliane Spiegler, Till Milde, Andreas Ziegler, Steffen Syrbe
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Item Description:In: Orphanet journal of rare diseases, 14 (2019), Nr. 96. pp. 1-13. ISSN 1750-1172
Physical Description:Online Resource