Safety and efficacy of mTOR inhibitor treatment in patients with tuberous sclerosis complex under 2 years of age: a multicenter retrospective study - Saffari, Afshin; Brösse, Ines; Tilburg, Cornelis M. van; Hoffmann, Georg F.; Kölker, Stefan; Witt, Olaf; Milde, Till; Ziegler, Andreas; Syrbe, Steffen (BioMed Central, 2019)
In: Orphanet journal of rare diseases, 14 (2019), Nr. 96. pp. 1-13. ISSN 1750-1172