Autologous ex vivo lentiviral gene therapy for adenosine deaminase deficiency
Original Article from The New England Journal of Medicine — Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency
Gespeichert in:
| Hauptverfasser: | , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , |
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| Dokumenttyp: | Article (Journal) |
| Sprache: | Englisch |
| Veröffentlicht: |
May 11, 2021
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| In: |
The New England journal of medicine
Year: 2021, Jahrgang: 384, Heft: 21, Pages: 2002-2013 |
| ISSN: | 1533-4406 |
| DOI: | 10.1056/NEJMoa2027675 |
| Online-Zugang: | Verlag, lizenzpflichtig, Volltext: https://doi.org/10.1056/NEJMoa2027675 Verlag, lizenzpflichtig, Volltext: https://www.nejm.org/doi/10.1056/NEJMoa2027675 
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| Verfasserangaben: | D.B. Kohn, C. Both, K.L. Shaw, J. Xu-Bayford, E. Garabedian, V. Trevisan, D.A. Carbonaro-Sarracino, K. Soni, D. Terrazas, K. Snell, A. Ikeda, D. Leon-Rico, T.B. Moore, K.F. Buckland, A.J. Shah, K.C. Gilmour, S. De Oliveira, C. Rivat, G.M. Crooks, N. Izotova, J. Tse, S. Adams, S. Shupien, H. Ricketts, A. Davila, C. Uzowuru, A. Icreverzi, P. Barman, B. Campo Fernandez, R.P. Hollis, M. Coronel, A. Yu, K.M. Chun, C.E. Casas, R. Zhang, S. Arduini, F. Lynn, M. Kudari, A. Spezzi, M. Zahn, R. Heimke, I. Labik, R. Parrott, R.H. Buckley, L. Reeves, K. Cornetta, R. Sokolic, M. Hershfield, M. Schmidt, F. Candotti, H.L. Malech, A.J. Thrasher, and H.B. Gaspar |
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| 520 | |a Original Article from The New England Journal of Medicine — Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency | ||
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