mRNA-based therapy proves superior to the standard of care for treating hereditary tyrosinemia 1 in a mouse model

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Bibliographic Details
Main Authors: Cacicedo, Maximiliano L. (Author) , Weinl-Tenbruck, Christine (Author) , Frank, Daniel (Author) , Wirsching, Sebastian (Author) , Straub, Beate Katharina (Author) , Hauke, Jana (Author) , Okun, Jürgen G. (Author) , Horscroft, Nigel (Author) , Hennermann, Julia B. (Author) , Zepp, Fred (Author) , Chevessier-Tünnesen, Frédéric (Author) , Gehring, Stephan (Author)
Format: Article (Journal)
Language:English
Published: September 2022
In: Molecular therapy. Methods & clinical development
Year: 2022, Volume: 26, Pages: 294-308
ISSN:2329-0501
DOI:10.1016/j.omtm.2022.07.006
Online Access:Verlag, lizenzpflichtig, Volltext: https://doi.org/10.1016/j.omtm.2022.07.006
Verlag, lizenzpflichtig, Volltext: https://www.sciencedirect.com/science/article/pii/S2329050122000985?via%3Dihub
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Author Notes:Maximiliano L. Cacicedo, Christine Weinl-Tenbruck, Daniel Frank, Sebastian Wirsching, Beate K. Straub, Jana Hauke, Jürgen G. Okun, Nigel Horscroft, Julia B. Hennermann, Fred Zepp, Frédéric Chevessier-Tünnesen and Stephan Gehring
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Item Description:Gesehen am 13.02.2023
Physical Description:Online Resource
ISSN:2329-0501
DOI:10.1016/j.omtm.2022.07.006