Gene therapy for aromatic L-amino acid decarboxylase deficiency: requirements for safe application and knowledge-generating follow-up - Roubertie, Agathe; Opladen, Thomas; Brennenstuhl, Heiko; Kuseyri Hübschmann, Oya; Flint, Lisa; Willemsen, Michel A.; Leuzzi, Vincenzo; Cazorla, Angels Garcia; Kurian, Manju A.; François-Heude, Marie Céline; Hwu, Paul; Zeev, Bruria Ben; et al. (Journal of inherited metabolic disease, 2023)
Gesehen am 09.08.2023