Treatment of infantile-onset Pompe disease in a rat model with muscle-directed AAV gene therapy - Muñoz, Sergio; Bertolin, Joan; Jimenez, Veronica; Jaén, Maria Luisa; Garcia, Miquel; Pujol, Anna; Vilà, Laia; Sacristan, Victor; Barbon, Elena; Ronzitti, Giuseppe; El Andari, Jihad; Tulalamba, Warut; et al. (Molecular metabolism, 2024)
Online verfügbar 10 February 2024, Version des Artikels 15 February 2024