Pre-clinical development of AP4B1 gene replacement therapy for hereditary spastic paraplegia type 47 - Wiseman, Jessica P.; Scarrott, Joseph M; Alves-Cruzeiro, João; Saffari, Afshin; Böger, Cedric; Karyka, Evangelia; Dawes, Emily; Davies, Alexandra K; Marchi, Paolo M; Graves, Emily; Fernandes, Fiona; Yang, Zih-Liang; et al. (EMBO molecular medicine, 2024)
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