Cognitive function in SMA patients with 2 or 3 SMN2 copies treated with SMN-modifying or gene addition therapy during the first year of life - Steffens, Paula; Weiss, Deike; Perez, Anna; Appel, Manuel; Weber, Philipp; Weiss, Claudia; Stoltenburg, Corinna; Ehinger, Ute; von der Hagen, Maja; Schallner, Jens; Claussen, Birte; Lode, Ilka; et al. (European journal of paediatric neurology, 2024)
Online verfügbar: 8. Mai 2024, Artikelversion: 20. Mai 2024