Primary CD34+ cells of patients with vacuoles, E1 enzyme, X-linked, autoinflammatory, somatic (VEXAS) syndrome are highly sensitive to targeted treatment with TAK-243: research letter

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Main Authors: Nowak, Daniel (Author) , Demmerle, Marie (Author) , Klär, Alessa (Author) , Streuer, Alexander (Author) , Riabov, Vladimir (Author) , Altrock, Eva (Author) , Rapp, Felicitas (Author) , Belzer, Ann-Christin (Author) , Klink, Teresa (Author) , Hahn, Meret (Author) , Hofmann, Franziska (Author) , Nowak, Verena (Author) , Weimer, Nadine (Author) , Obländer, Julia (Author) , Palme, Iris (Author) , Göl, Melda (Author) , Darwich, Ali (Author) , Steiner, Laurenz (Author) , Abba, Mohammed L. (Author) , Metzgeroth, Georgia (Author) , Hofmann, Wolf-Karsten (Author) , Schmitt, Nanni (Author)
Format: Article (Journal) Editorial
Language:English
Published: December 2025
In: British journal of haematology
Year: 2025, Volume: 207, Issue: 6, Pages: 2558-2562
ISSN:1365-2141
DOI:10.1111/bjh.70203
Online Access:Verlag, kostenfrei, Volltext: https://doi.org/10.1111/bjh.70203
Verlag, kostenfrei, Volltext: https://onlinelibrary.wiley.com/doi/abs/10.1111/bjh.70203
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Author Notes:Daniel Nowak, Marie Demmerle, Alessa Klär, Alexander Streuer, Vladimir Riabov, Eva Altrock, Felicitas Rapp, Ann-Christin Belzer, Teresa Klink, Meret Hahn, Franziska Hofmann, Verena Nowak, Nadine Weimer, Julia Obländer, Iris Palme, Melda Göl, Ali Darwich, Laurenz Steiner, Mohammed Abba, Georgia Metzgeroth, Wolf-Karsten Hofmann, Nanni Schmitt
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Item Description:Im Titel ist das Plus-Symbol hochgestellt
Erstmals veröffentlicht: 12. Oktober 2025
Gesehen am 25.11.2025
Physical Description:Online Resource
ISSN:1365-2141
DOI:10.1111/bjh.70203