Primary CD34+ cells of patients with vacuoles, E1 enzyme, X-linked, autoinflammatory, somatic (VEXAS) syndrome are highly sensitive to targeted treatment with TAK-243: research letter
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| Main Authors: | , , , , , , , , , , , , , , , , , , , , , |
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| Format: | Article (Journal) Editorial |
| Language: | English |
| Published: |
December 2025
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| In: |
British journal of haematology
Year: 2025, Volume: 207, Issue: 6, Pages: 2558-2562 |
| ISSN: | 1365-2141 |
| DOI: | 10.1111/bjh.70203 |
| Online Access: | Verlag, kostenfrei, Volltext: https://doi.org/10.1111/bjh.70203 Verlag, kostenfrei, Volltext: https://onlinelibrary.wiley.com/doi/abs/10.1111/bjh.70203 |
| Author Notes: | Daniel Nowak, Marie Demmerle, Alessa Klär, Alexander Streuer, Vladimir Riabov, Eva Altrock, Felicitas Rapp, Ann-Christin Belzer, Teresa Klink, Meret Hahn, Franziska Hofmann, Verena Nowak, Nadine Weimer, Julia Obländer, Iris Palme, Melda Göl, Ali Darwich, Laurenz Steiner, Mohammed Abba, Georgia Metzgeroth, Wolf-Karsten Hofmann, Nanni Schmitt |
| Item Description: | Im Titel ist das Plus-Symbol hochgestellt Erstmals veröffentlicht: 12. Oktober 2025 Gesehen am 25.11.2025 |
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| Physical Description: | Online Resource |
| ISSN: | 1365-2141 |
| DOI: | 10.1111/bjh.70203 |