Current treatment decisions in cardiac transthyretin amyloidosis: a multicentre analysis
The efficacy of transthyretin stabilisation in cardiac transthyretin amyloidosis (ATTR-CM) has been demonstrated in a clinical trial setting, but little is known about treatment decision-making in the real world. Particularly, initiating or discontinuing specific therapy is challenging in early and...
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| Main Authors: | , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , , |
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| Format: | Article (Journal) |
| Language: | English |
| Published: |
26 January 2026
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| In: |
Clinical research in cardiology
Year: 2026, Volume: 115, Issue: 5, Pages: 862-874 |
| ISSN: | 1861-0692 |
| DOI: | 10.1007/s00392-026-02848-z |
| Online Access: | Verlag, kostenfrei, Volltext: https://doi.org/10.1007/s00392-026-02848-z |
| Author Notes: | Daniel Lavall, Katharina Knoll, Sebastian Spethmann, Katrin Hahn, Gina Barzen, Ephraim B. Winzer, Stefanie Jellinghaus, Lisa K. Schöner, Monique Tröbs, Dominik Kauffmann, Nora Donhauser, Lars Michel, Julia Vogel, Tienush Rassaf, Maria Papathanasiou, Lara S. Schlender, David M. Leistner, Birgit Aßmus, Bernhard Unsöld, Larissa Bühner, Fabian aus dem Siepen, Eva Hofmann, Christian Nagel, Ingrid Kindermann, Angela Zimmer, Roman Pfister, Matthieu Schäfer, Natascha Majunke, Irina Müller-Kozarez, Heribert Schunkert, Patrick Fuchs, Stéphanie K. Schwarting, Yuliyan Metodiev, Selen Alieva, Ali Yilmaz, Alexandru Zlibut, Julian Mustroph, Maria Tafelmeier, Thomas Krammer, Stefan Störk, Aikaterini Papagianni, Maximilian J. Steinhardt, Vladimir Cejka, Caroline Morbach, Teresa Trenkwalder |
| Summary: | The efficacy of transthyretin stabilisation in cardiac transthyretin amyloidosis (ATTR-CM) has been demonstrated in a clinical trial setting, but little is known about treatment decision-making in the real world. Particularly, initiating or discontinuing specific therapy is challenging in early and advanced disease. We evaluated current decision pathways for tafamidis in ATTR-CM. |
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| Item Description: | Gesehen am 24.04.2026 |
| Physical Description: | Online Resource |
| ISSN: | 1861-0692 |
| DOI: | 10.1007/s00392-026-02848-z |