Current treatment decisions in cardiac transthyretin amyloidosis: a multicentre analysis

The efficacy of transthyretin stabilisation in cardiac transthyretin amyloidosis (ATTR-CM) has been demonstrated in a clinical trial setting, but little is known about treatment decision-making in the real world. Particularly, initiating or discontinuing specific therapy is challenging in early and...

Full description

Saved in:
Bibliographic Details
Main Authors: Lavall, Daniel (Author) , Knoll, Katharina (Author) , Spethmann, Sebastian (Author) , Hahn, Katrin (Author) , Barzen, Gina (Author) , Winzer, Ephraim B. (Author) , Jellinghaus, Stefanie (Author) , Schöner, Lisa K. (Author) , Tröbs, Monique (Author) , Kauffmann, Dominik (Author) , Donhauser, Nora (Author) , Michel, Lars (Author) , Vogel, Julia (Author) , Rassaf, Tienush (Author) , Papathanasiou, Maria (Author) , Schlender, Lara S. (Author) , Leistner, David M. (Author) , Aßmus, Birgit (Author) , Unsöld, Bernhard (Author) , Bühner, Larissa (Author) , Siepen, Fabian aus dem (Author) , Hofmann, Eva Catarina Maria (Author) , Nagel, Christian (Author) , Kindermann, Ingrid (Author) , Zimmer, Angela (Author) , Pfister, Roman (Author) , Schäfer, Matthieu (Author) , Majunke, Natascha (Author) , Müller-Kozarez, Irina (Author) , Schunkert, Heribert (Author) , Fuchs, Patrick (Author) , Schwarting, Stéphanie K. (Author) , Metodiev, Yuliyan (Author) , Alieva, Selen (Author) , Yilmaz, Ali (Author) , Zlibut, Alexandru (Author) , Mustroph, Julian (Author) , Tafelmeier, Maria (Author) , Krammer, Thomas (Author) , Störk, Stefan (Author) , Papagianni, Aikaterini (Author) , Steinhardt, Maximilian J. (Author) , Cejka, Vladimir (Author) , Morbach, Caroline (Author) , Trenkwalder, Teresa (Author)
Format: Article (Journal)
Language:English
Published: 26 January 2026
In: Clinical research in cardiology
Year: 2026, Volume: 115, Issue: 5, Pages: 862-874
ISSN:1861-0692
DOI:10.1007/s00392-026-02848-z
Online Access:Verlag, kostenfrei, Volltext: https://doi.org/10.1007/s00392-026-02848-z
Get full text
Author Notes:Daniel Lavall, Katharina Knoll, Sebastian Spethmann, Katrin Hahn, Gina Barzen, Ephraim B. Winzer, Stefanie Jellinghaus, Lisa K. Schöner, Monique Tröbs, Dominik Kauffmann, Nora Donhauser, Lars Michel, Julia Vogel, Tienush Rassaf, Maria Papathanasiou, Lara S. Schlender, David M. Leistner, Birgit Aßmus, Bernhard Unsöld, Larissa Bühner, Fabian aus dem Siepen, Eva Hofmann, Christian Nagel, Ingrid Kindermann, Angela Zimmer, Roman Pfister, Matthieu Schäfer, Natascha Majunke, Irina Müller-Kozarez, Heribert Schunkert, Patrick Fuchs, Stéphanie K. Schwarting, Yuliyan Metodiev, Selen Alieva, Ali Yilmaz, Alexandru Zlibut, Julian Mustroph, Maria Tafelmeier, Thomas Krammer, Stefan Störk, Aikaterini Papagianni, Maximilian J. Steinhardt, Vladimir Cejka, Caroline Morbach, Teresa Trenkwalder
Description
Summary:The efficacy of transthyretin stabilisation in cardiac transthyretin amyloidosis (ATTR-CM) has been demonstrated in a clinical trial setting, but little is known about treatment decision-making in the real world. Particularly, initiating or discontinuing specific therapy is challenging in early and advanced disease. We evaluated current decision pathways for tafamidis in ATTR-CM.
Item Description:Gesehen am 24.04.2026
Physical Description:Online Resource
ISSN:1861-0692
DOI:10.1007/s00392-026-02848-z