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2024 update: european consensus statement on gene therapy for spinal muscular atrophy by Kirschner, Janbernd (Author) , Bernert, Günther (Author) , Butoianu, Nina (Author) , De Waele, Liesbeth (Author) , Fattal-Valevski, Aviva (Author) , Haberlova, Jana (Author) , Moreno, Teresa (Author) , Klein, Andrea (Author) , Kostera-Pruszczyk, Anna (Author) , Mercuri, Eugenio (Author) , Quijano-Roy, Susana (Author) , Sejersen, Thomas (Author) , Tizzano, Eduardo F. (Author) , van der Pol, W Ludo (Author) , Wallace, Sean (Author) , Zafeiriou, Dimitrios (Author) , Ziegler, Andreas (Author) , Muntoni, Francesco (Author) , Servais, Laurent (Author) ,
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