Search Results - "Gene therapy"

Systematic review of mitochondrial dysfunction and oxidative stress in aging: a focus on neuromuscular junctions by Chai, Senlin (Author) , Zhang, Ning (Author) , Cui, Can (Author) , Bao, Zhengyuan (Author) , Wang, Qianjin (Author) , Lin, Wujian (Author) , Wong, Ronald Man Yeung (Author) , Law, Sheung Wai (Author) , Schönmehl, Rebecca (Author) , Brochhausen, Christoph (Author) , Cheung, Wing Hoi (Author) ,

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Optimizing the anesthetic care of patients with aromatic l-amino acid decarboxylase deficiency by Kanjia, Megha K. (Author) , Jooste, Edmund H. (Author) , Illig, Melissa (Author) , Neifeld Capps, Jennifer (Author) , Eisner, Christoph (Author) , Fan, Shou Zen (Author) , Lenarczyk, Jerzy (Author) , Wojdacz, Rafał (Author) ,

Subjects: “…gene therapy…”

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Gene therapy in transfusion-dependent non-β0/β0 genotype β-thalassemia first real-world experience of beti-cel by Mirza, Adil (Author) , Ritsert, Mona-Lisa (Author) , Tao, Gloria (Author) , Thakar, Himal (Author) , Lobitz, Stephan (Author) , Heine, Sabine (Author) , Koscher, Leila (Author) , Dürken, Matthias (Author) , Schmitt, Anita (Author) , Schmitt, Michael (Author) , Pavel, Petra (Author) , Laier, Sascha (Author) , Jakoby-Gaide, Donate (Author) , Greil, Johann (Author) , Kunz, Joachim (Author) , Kulozik, Andreas (Author) ,

“…Gene therapy in transfusion-dependent non-beta 0 /beta 0 genotype beta-thalassemia…”

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State of the art and perspectives of gene therapy in heart failure a scientific statement of the Heart Failure Association of the ESC, the ESC Council on Cardiovascular Genomics and the ESC Working Group on Myocardial & Pericardial Diseases by Linthout, Sophie Van (Author) , Stellos, Konstantinos (Author) , Giacca, Mauro (Author) , Bertero, Edoardo (Author) , Cannata, Antonio (Author) , Carrier, Lucie (Author) , Garcia-Pavia, Pablo (Author) , Ghigo, Alessandra (Author) , González, Arantxa (Author) , Haugaa, Kristina H. (Author) , Imazio, Massimo (Author) , Lopes, Luis R. (Author) , Most, Patrick (Author) , Pollesello, Piero (Author) , Schunkert, Heribert (Author) , Streckfuss-Bömeke, Katrin (Author) , Thum, Thomas (Author) , Tocchetti, Carlo Gabriele (Author) , Tschöpe, Carsten (Author) , van der Meer, Peter (Author) , van Rooij, Eva (Author) , Metra, Marco (Author) , Rosano, Giuseppe M.C. (Author) , Heymans, Stephane (Author) ,

Subjects: “…Gene therapy…”

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Regional distribution of polymorphisms associated to the disease-causing gene of spinocerebellar ataxia type 3 by Elter, Tim (Author) , Sturm, Daniel (Author) , Santana, Magda M. (Author) , Schaprian, Tamara (Author) , Raposo, Mafalda (Author) , Melo, Ana Rosa Vieira (Author) , Lima, Manuela (Author) , Koyak, Berkan (Author) , Oender, Demet (Author) , Grobe-Einsler, Marcus (Author) , Lopes, Sara (Author) , Silva, Patrick (Author) , de Almeida, Luís Pereira (Author) , Giunti, Paola (Author) , Garcia-Moreno, Hector (Author) , Nethisinhe, Suran (Author) , de Vries, Jeroen (Author) , van de Warrenburg, Bart P. (Author) , van Gaalen, Judith (Author) , Synofzik, Matthis (Author) , Schöls, Ludger (Author) , Reetz, Kathrin (Author) , Erdlenbruch, Friedrich (Author) , Jacobi, Heike (Author) , Infante, Jon (Author) , Rieß, Olaf (Author) , Klockgether, Thomas (Author) , Timmann, Dagmar (Author) , Thieme, Andreas (Author) , Faber, Jennifer (Author) , Hübener-Schmid, Jeannette (Author) ,

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Gene therapy targeting INa to treat life-threatening arrhythmias beyond proof-of-concept? by Lugenbiel, Patrick (Author)

“…Gene therapy targeting I Na to treat life-threatening arrhythmias…”

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AAV vector engineering for human aorta transduction: becoming a smooth operator by Rapti, Kleopatra (Author) , Grimm, Dirk (Author) ,

Subjects: “…Gene therapy…”

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Thrombotic microangiopathy following gene therapy for 5q-spinal muscular atrophy by Gontijo Camelo, Clara (Author) , Mendonça, Rodrigo Holanda (Author) , Moreno, Cristiane Araújo Martins (Author) , Ferreira, Juliana Caires Oliveira Achili (Author) , Ortega, Adriana Banzzatto (Author) , van der Linden, Vanessa (Author) , Campos, Rejane Souza Macedo (Author) , van der Linden, Helio (Author) , da Cunha, Natalia Spinola Costa (Author) , Gurgel-Giannetti, Juliana (Author) , Chaves, Janaina Monteiro (Author) , Miranda, Silvana Maria Carvalho (Author) , Ziegler, Andreas (Author) , Zanoteli, Edmar (Author) ,

Subjects: “…Gene therapy…”

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hInGeTox: a human-based in vitro platform to evaluate lentivirus/host interactions that contribute to genotoxicity by Suleman, Saqlain (Author) , Alhaque, Sharmin (Author) , Guo, Andrew (Author) , Zhang, Huairen (Author) , Payne, Annette (Author) , Zahn, Marco (Author) , Fawaz, Serena (Author) , Khalifa, Mohammad S. (Author) , Jobling, Susan (Author) , Hay, David (Author) , Franco, Matteo (Author) , Fronza, Raffaele (Author) , Wang, Wei (Author) , Strobel-Freidekind, Olga (Author) , Deichmann, Annette (Author) , Takeuchi, Yasuhiro (Author) , Gil-Farina, Irene (Author) , Klapwijk, Jan (Author) , Perera, Stefany (Author) , Schmidt, Manfred (Author) , Themis, Michael (Author) ,

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Direct translation of incoming retroviral genomes by Köppke, Julia (Author) , Keller, Luise-Elektra (Author) , Stuck, Michelle (Author) , Arnow, Nicolas D. (Author) , Bannert, Norbert (Author) , Döllinger, Jörg (Author) , Cingöz, Oya (Author) ,

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Towards a light-mediated gene therapy for the eye using caged ethinylestradiol and the inducible Cre/lox system by Kiy, Zoe (Author) , Chaud, Juliane (Author) , Xu, Liang (Author) , Brandhorst, Eric (Author) , Kamali, Tschackad (Author) , Vargas, Carolyn (Author) , Keller, Sandro (Author) , Hong, Huixiao (Author) , Specht, Alexandre (Author) , Cambridge, Sidney (Author) ,

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Regnase-1 overexpression as a therapeutic approach of Marfan syndrome by Noormalal, Marie (Author) , Schmiedel, Nesrin (Author) , Bozoglu, Tarik (Author) , Matzen, Andrea (Author) , Hille, Susanne (Author) , Basha, Dima Ibrahim (Author) , Vijaya Shetty, Prithviraj Manohar (Author) , Wolf, Anja (Author) , Zaradzki, Marcin (Author) , Arif, Rawa (Author) , Pühler, Thomas (Author) , Lutter, Georg (Author) , Wagner, Andreas H. (Author) , Kupatt, Christian (Author) , Frank, Derk (Author) , Frey, Norbert (Author) , Remes, Anca (Author) , Müller, Oliver J. (Author) ,

Subjects: “…gene therapy…”

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S100A1: a promising therapeutic target for heart failure by Noll, Dorothea (Author) , Kehr, Dorothea (Author) , Most, Patrick (Author) , Ritterhoff, Julia (Author) ,

Subjects: “…gene therapy…”

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Treatment of infantile-onset Pompe disease in a rat model with muscle-directed AAV gene therapy by Muñoz, Sergio (Author) , Bertolin, Joan (Author) , Jimenez, Veronica (Author) , Jaén, Maria Luisa (Author) , Garcia, Miquel (Author) , Pujol, Anna (Author) , Vilà, Laia (Author) , Sacristan, Victor (Author) , Barbon, Elena (Author) , Ronzitti, Giuseppe (Author) , El Andari, Jihad (Author) , Tulalamba, Warut (Author) , Pham, Quang Hong (Author) , Ruberte, Jesus (Author) , VandenDriessche, Thierry (Author) , Chuah, Marinee K. (Author) , Grimm, Dirk (Author) , Mingozzi, Federico (Author) , Bosch, Fatima (Author) ,

Subjects: “…Gene therapy…”

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One gene to rule them all: clinical perspectives of a potent suppressor of cytokine signaling : SOCS1 by Körholz, Julia Christine (Author) , Chen, Lan-Sun (Author) , Strauß, Timmy (Author) , Schuetz, Catharina (Author) , Dalpke, Alexander (Author) ,

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Newborn screening for aromatic l-amino acid decarboxylase deficiency: strategies, results, and implication for prevalence calculations by Reischl-Hajiabadi, Anna Theresa (Author) , Okun, Jürgen G. (Author) , Kohlmüller, Dirk (Author) , Manukjan, Georgi (Author) , Hegert, Sebastian (Author) , Durner, Jürgen (Author) , Schuhmann, Elfriede (Author) , Hörster, Friederike (Author) , Mütze, Ulrike (Author) , Feyh, Patrik (Author) , Hoffmann, Georg F. (Author) , Röschinger, Wulf (Author) , Janzen, Nils (Author) , Opladen, Thomas (Author) ,

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Cardiomyocyte-specific RXFP1 overexpression protects against pressure overload-induced cardiac dysfunction independently of relaxin by Wingert, Julia (Author) , Meinhardt, Eric (Author) , Sasipong, Nuttarak (Author) , Pott, Marcel (Author) , Lederer, Christoph (Author) , Torre, Carolina de la (Author) , Sticht, Carsten (Author) , Most, Patrick (Author) , Katus, Hugo (Author) , Frey, Norbert (Author) , Raake, Philip (Author) , Schlegel, Philipp (Author) ,

Subjects: “…Gene therapy…”

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Clinical and molecular outcomes from the 5-Year natural history study of SSADH deficiency, a model metabolic neurodevelopmental disorder by Tokatly Latzer, Itay (Author) , Roullet, Jean-Baptiste (Author) , Afshar-Saber, Wardiya (Author) , Lee, Henry H. C. (Author) , Bertoldi, Mariarita (Author) , McGinty, Gabrielle E. (Author) , DiBacco, Melissa L. (Author) , Arning, Erland (Author) , Tsuboyama, Melissa (Author) , Rotenberg, Alexander (Author) , Opladen, Thomas (Author) , Jeltsch, Kathrin (Author) , García-Cazorla, Àngels (Author) , Julià-Palacios, Natalia (Author) , Gibson, K. Michael (Author) , Sahin, Mustafa (Author) , Pearl, Phillip L. (Author) ,

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Design and characterization of a gene-encoding DNA nanoparticle in a cell-free transcription-translation system by Galvan, Angelica Rose (Author) , Green, Christopher M. (Author) , Hooe, Shelby L. (Author) , Oktay, Esra (Author) , Thakur, Meghna (Author) , Díaz, Sebastián A. (Author) , Veneziano, Remi (Author) , Medintz, Igor L. (Author) , Mathur, Divita (Author) ,

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S100A1’s single cysteine is an indispensable redox switch for the protection against diastolic calcium waves in cardiomyocytes by Seitz, Andreas (Author) , Busch, Martin (Author) , Krömer, Jasmin (Author) , Schneider, Andrea (Author) , Simon, Stephanie (Author) , Jungmann, Andreas (Author) , Katus, Hugo (Author) , Most, Patrick (Author) , Ritterhoff, Julia (Author) ,

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