Cas9-specific immune responses compromise local and systemic AAV CRISPR therapy in multiple dystrophic canine models
by Hakim, Chady H. (Author)
, Kumar, Sandeep R. P. (Author)
, Pérez-López, Dennis O. (Author)
, Wasala, Nalinda B. (Author)
, Zhang, Dong (Author)
, Yue, Yongping (Author)
, Teixeira, James (Author)
, Pan, Xiufang (Author)
, Zhang, Keqing (Author)
, Million, Emily D. (Author)
, Nelson, Christopher E. (Author)
, Metzger, Samantha (Author)
, Han, Jin (Author)
, Louderman, Jacqueline A. (Author)
, Schmidt, Florian (Author)
, Feng, Feng (Author)
, Grimm, Dirk (Author)
, Smith, Bruce F. (Author)
, Yao, Gang (Author)
, Yang, N. Nora (Author)
, Gersbach, Charles A. (Author)
, Chen, Shi-jie (Author)
, Herzog, Roland W. (Author)
, Duan, Dongsheng (Author)
,
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