Successful combination of cequential gene therapy and rescue allo-HSCT in two children with X-CGD: importance of timing

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Bibliographic Details
Main Authors: Siler, Ulrich (Author) , Paruzynski, Anna (Author) , Holtgreve-Grez, Heidi (Author) , Jauch, Anna (Author) , Kalle, Christof von (Author) , Schmidt, Manfred (Author)
Format: Article (Journal)
Language:English
Published: 2015
In: Current gene therapy
Year: 2015, Volume: 15, Issue: 4, Pages: 416-427
ISSN:1875-5631
DOI:10.2174/1566523215666150515145255
Online Access:Verlag, Volltext: http://dx.doi.org/10.2174/1566523215666150515145255
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Author Notes:Ulrich Siler, Anna Paruzynski, Heidi Holtgreve-Grez, Elena Kuzmenko, Ulrike Koehl, Eleonore D. Renner, Canan Alhan, Arjan A. van de Loosdrecht, Joachim Schwäble, Thomas Pfluger, Joelle Tchinda, Markus Schmugge, Anna Jauch, Sonja Naundorf, Klaus Kühlcke, Gundula Notheis, Tayfun Güngor, Christof v. Kalle, Manfred Schmidt, Manuel Grez, Reinhard Seger, Janine Reichenbach
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Item Description:Gesehen am 04.01.2017
Physical Description:Online Resource
ISSN:1875-5631
DOI:10.2174/1566523215666150515145255