Patisiran, an RNAi therapeutic, for hereditary transthyretin amyloidosis
Original Article from The New England Journal of Medicine - Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis
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| Main Authors: | , |
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| Format: | Article (Journal) |
| Language: | English |
| Published: |
July 5, 2018
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| In: |
The New England journal of medicine
Year: 2018, Volume: 379, Issue: 1, Pages: 11-21 |
| ISSN: | 1533-4406 |
| DOI: | 10.1056/NEJMoa1716153 |
| Online Access: | Verlag, Volltext: https://doi.org/10.1056/NEJMoa1716153 Verlag, Volltext: https://www.nejm.org/doi/10.1056/NEJMoa1716153 |
| Author Notes: | D. Adams, A. Gonzalez-Duarte, W.D. O’Riordan, C.-C. Yang, M. Ueda, A.V. Kristen, I. Tournev, H.H. Schmidt, T. Coelho, J.L. Berk, K.-P. Lin, G. Vita, S. Attarian, V. Planté-Bordeneuve, M.M. Mezei, J.M. Campistol, J. Buades, T.H. Brannagan III, B.J. Kim, J. Oh, Y. Parman, Y. Sekijima, P.N. Hawkins, S.D. Solomon, M. Polydefkis, P.J. Dyck, P.J. Gandhi, S. Goyal, J. Chen, A.L. Strahs, S.V. Nochur, M.T. Sweetser, P.P. Garg, A.K. Vaishnaw, J.A. Gollob, and O.B. Suhr |
| Summary: | Original Article from The New England Journal of Medicine - Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis |
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| Item Description: | Gesehen am 07.05.2019 |
| Physical Description: | Online Resource |
| ISSN: | 1533-4406 |
| DOI: | 10.1056/NEJMoa1716153 |