Comparison of organoid swelling and in vivo biomarkers of CFTR function to determine effects of lumacaftor-ivacaftor in patients with cystic fibrosis homozygous for the F508del mutation

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Main Authors: Gräber, Simon Y. (Author) , van Mourik, Peter (Author) , Vonk, Annelotte M. (Author) , Kruisselbrink, Evelien (Author) , Hirtz, Stephanie (Author) , van der Ent, Cornelis K. (Author) , Mall, Marcus A. (Author) , Beekman, Jeffrey M. (Author)
Format: Article (Journal) Editorial
Language:English
Published: July 20, 2020
In: American journal of respiratory and critical care medicine
Year: 2020, Volume: 202, Issue: 11, Pages: 1589-1592
ISSN:1535-4970
DOI:10.1164/rccm.202004-1200LE
Online Access:Verlag, lizenzpflichtig, Volltext: https://doi.org/10.1164/rccm.202004-1200LE
Verlag, lizenzpflichtig, Volltext: https://www.atsjournals.org/doi/10.1164/rccm.202004-1200LE
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Author Notes:Simon Y. Graeber, Peter van Mourik, Annelotte M. Vonk, Evelien Kruisselbrink, Stephanie Hirtz, Cornelis K. van der Ent, Marcus A. Mall, and Jeffrey M. Beekman
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Item Description:Gesehen am 21.01.2021
Physical Description:Online Resource
ISSN:1535-4970
DOI:10.1164/rccm.202004-1200LE