Effect of long-term sepiapterin treatment on dietary phenylalanine tolerance in patients with phenylketonuria: interim results from the phase 3 APHENITY Extension Study
by Spronsen, F. J. van (Author)
, Peters, Heidi (Author)
, Margvelashvili, Lali (Author)
, Agladze, Dodo (Author)
, Schwartz, Ida Vanessa D. (Author)
, Giżewska, Maria (Author)
, Hamazaki, Takashi (Author)
, Guilder, Laura (Author)
, MacDonald, Anita (Author)
, Vijay, Suresh (Author)
, Inwood, Anita (Author)
, Minami, Maria (Author)
, Fjellbirkeland, Olivia (Author)
, Lund, Allan (Author)
, Lah, Melissa (Author)
, Thomas, Janet A. (Author)
, Longo, Nicola (Author)
, Kiykim, Ertuğrul (Author)
, Ishige, Mika (Author)
, Burlina, Alberto (Author)
, Bélanger-Quintana, Amaya (Author)
, Rutsch, Frank (Author)
, Opladen, Thomas (Author)
, Mungan, Halise (Author)
, Ezgü, Fatih (Author)
, Bratkovic, Drago (Author)
, Chakrapani, Anupam (Author)
, Ito, Tetsuya (Author)
, Guimas, Arlindo (Author)
, Zori, Roberto (Author)
, Tchan, Michel (Author)
, Sacharow, Stephanie (Author)
, Oliveira, Anabela (Author)
, Janeiro, Patricia (Author)
, Guerra, Ixiu-Cabrales (Author)
, Plana, Jaume Campistol (Author)
, Yıldız, Yılmaz (Author)
, Canda, Ebru (Author)
, Khan, Aneal (Author)
, Vockley, Jerry (Author)
, Breilyn, Margo Sheck (Author)
, Manti, Filippo (Author)
, Larkin, Alex (Author)
, Hughes, Catalina (Author)
, Liu, Emelline (Author)
, Gao, Lan (Author)
, Ingalls, Kimberly (Author)
, Smith, Neil (Author)
, Muntau, Ania C. (Author)
,
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