Search Results - Horber, Veronka

Efficacy and safety of gene therapy with onasemnogene abeparvovec in children with spinal muscular atrophy in the D-A-CH-region: a population-based observational study by Weiß, Claudia (Author) , Becker, Lena-Luise (Author) , Friese, Johannes (Author) , Blaschek, Astrid (Author) , Hahn, Andreas (Author) , Illsinger, Sabine (Author) , Schwartz, Oliver (Author) , Bernert, Günther (Author) , Hagen, Maja von der (Author) , Husain, Ralf A. (Author) , Goldhahn, Klaus (Author) , Kirschner, Janbernd (Author) , Pechmann, Astrid (Author) , Flotats-Bastardas, Marina (Author) , Schreiber, Gudrun (Author) , Schara, Ulrike (Author) , Plecko, Barbara (Author) , Trollmann, Regina (Author) , Horber, Veronka (Author) , Wilichowski, Ekkehard (Author) , Baumann, Matthias (Author) , Klein, Andrea (Author) , Eisenkölbl, Astrid (Author) , Köhler, Cornelia (Author) , Stettner, Georg M. (Author) , Cirak, Sebahattin (Author) , Hasselmann, Oswald (Author) , Kaindl, Angela M. (Author) , Garbade, Sven (Author) , Johannsen, Jessika (Author) , Ziegler, Andreas (Author) ,

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Newbornscreening SMA: from pilot project to nationwide screening in Germany by Müller-Felber, Wolfgang (Author) , Blaschek, Astrid (Author) , Schwartz, Oliver (Author) , Gläser, Dieter (Author) , Nennstiel, Uta (Author) , Brockow, Inken (Author) , Wirth, Brunhilde (Author) , Burggraf, Siegfried (Author) , Röschinger, Wulf (Author) , Becker, Marc (Author) , Durner, Jürgen (Author) , Eggermann, Katja (Author) , Kölbel, Heike (Author) , Müller, Christine (Author) , Hannibal, Iris (Author) , Olgemöller, Bernd (Author) , Schara, Ulrike (Author) , von Moers, Arpad (Author) , Trollmann, Regina (Author) , Johannssen, Jessika (Author) , Ziegler, Andreas (Author) , Cirak, Sebahattin (Author) , Hahn, Andreas (Author) , von der Hagen, Maja (Author) , Weiss, Claudia (Author) , Schreiber, Gudrun (Author) , Flotats-Bastardas, Marina (Author) , Hartmann, Hans (Author) , Illsinger, Sabine (Author) , Pechmann, Astrid (Author) , Horber, Veronka (Author) , Kirschner, Janbernd (Author) , Köhler, Cornelia (Author) , Winter, Benedikt (Author) , Friese, Johannes (Author) , Vill, Katharina (Author) ,

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Gene replacement therapy with onasemnogene abeparvovec in children with spinal muscular atrophy aged 24 months or younger and bodyweight up to 15 kg: an observational cohort study by Weiß, Claudia (Author) , Ziegler, Andreas (Author) , Becker, Lena-Luise (Author) , Johannsen, Jessika (Author) , Brennenstuhl, Heiko (Author) , Schreiber, Gudrun (Author) , Flotats-Bastardas, Marina (Author) , Stoltenburg, Corinna (Author) , Hartmann, Hans (Author) , Illsinger, Sabine (Author) , Denecke, Jonas (Author) , Pechmann, Astrid (Author) , Müller-Felber, Wolfgang (Author) , Vill, Katharina (Author) , Blaschek, Astrid (Author) , Smitka, Martin (Author) , van der Stam, Lieske (Author) , Weiss, Katja (Author) , Winter, Benedikt (Author) , Goldhahn, Klaus (Author) , Plecko, Barbara (Author) , Horber, Veronka (Author) , Bernert, Günther (Author) , Husain, Ralf A (Author) , Rauscher, Christian (Author) , Trollmann, Regina (Author) , Garbade, Sven (Author) , Hahn, Andreas (Author) , von der Hagen, Maja (Author) , Kaindl, Angela M (Author) ,

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Handlungsempfehlungen zur Gentherapie der spinalen Muskelatrophie mit Onasemnogene Abeparvovec - AVXS-101: Konsensuspapier der deutschen Vertretung der Gesellschaft für Neuropädi... by Ziegler, Andreas (Author) , Wilichowski, Ekkehard (Author) , Schara, Ulrike (Author) , Hahn, Andreas (Author) , Müller-Felber, Wolfgang (Author) , Johannsen, Jessika (Author) , Hagen, Maja von der (Author) , Moers, Arpad von (Author) , Stoltenburg, Corinna (Author) , Saffari, Afshin (Author) , Walter, Maggie C. (Author) , Husain, Ralf (Author) , Pechmann, Astrid (Author) , Köhler, Cornelia (Author) , Horber, Veronka (Author) , Schwartz, Oliver (Author) , Kirschner, Janbernd (Author) ,

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